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Neural precursor cell cultures from GM2 gangliosidosis animal models recapitulate the biochemical and molecular hallmarks of the brain pathology

Sabata Martino, Ilaria Di Girolamo, Chiara Cavazzin, Roberto Tiribuzi, Rossella Galli, Anna Rivaroli, Manuela Valsecchi, Konrad Sandhoff, Sandro Sonnino, Angelo Vescovi, Angela Gritti, Aldo Orlacchio

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Biochemistry, Genetics and Molecular Biology