Project Details
| Status | Active |
|---|---|
| Effective start/end date | 3/26/25 → … |
An open-label single center, single participant study of an experimental antisense oligonucleotide treatment for amyotrophic lateral sclerosis (ALS) due to TARDBP (TDP-43) genetic mutation
- Shroff, Sheetal (PI)
- Appel, Stanley H. (Key Personnel)
Project: Clinical Trial