Projects per year
Projects
Search results
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TRACK-ALS-001
Masdeu, J. C., Appel, S. H., Kocharian, A., Nakawah, M. O., Pascual, B., Thonhoff, J. R. & Yu, M.
8/10/15 → …
Project: Clinical Trial
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Genomic Translation for ALS Clinical Care
Appel, S. H., Greene, E. P., Shroff, S. & Thonhoff, J. R.
4/1/17 → …
Project: Clinical Trial
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T-Reg Leukapheresis_2.0_ALSAFAC_807
Appel, S. H., Bruno, I. G. & Thonhoff, J. R.
8/1/18 → 1/31/22
Project: Non Profit
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Neuromuscular Observational Research (MOVR) Data Hub Protocol
Greene, E. P., Appel, S. H., Shroff, S. & Thonhoff, J. R.
5/17/19 → …
Project: Clinical Trial
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T-regulatory Cells in ALS (Tregs in ALS)
Thonhoff, J. R., Appel, S. H., Greene, E. P. & Shroff, S.
8/15/19 → …
Project: Clinical Trial
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Safety and Efficacy Study of Ravulizumab in Adults With Generalized Myasthenia Gravis
Greene, E. P., Appel, S. H., Liao, B., Shroff, S. & Thonhoff, J. R.
9/17/19 → …
Project: Clinical Trial
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Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1: END-DM1
Greene, E. P., Ashizawa, T., Shroff, S. & Thonhoff, J. R.
12/17/19 → …
Project: Clinical Trial
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Phase III Efficacy, Safety, and Tolerability Study of HYQVIA/HyQvia and GAMMAGARD LIQUID/KIOVIG in CIDP
Greene, E. P., Appel, S. H., Shroff, S. & Thonhoff, J. R.
4/15/20 → …
Project: Clinical Trial
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Massachusetts General Hospital Healey Center for ALS - Healey ALS Platform Trial
Appel, S. H., Greene, E. P., Shroff, S. & Thonhoff, J. R.
7/24/20 → 12/31/22
Project: Non Profit
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HEALEY ALS Platform Trial - Regimen-Specific Appendix A - For 0.3mh/kg SC zilucoplan administered once daily and placebo
Appel, S. H., Greene, E. P., Liao, B., Shroff, S. & Thonhoff, J. R.
7/24/20 → 7/23/25
Project: Non Profit
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HEALEY ALS Platform Trial - Regimen-Specific Appendix B - For verdiperstat (also known as BHV-3241)
Appel, S. H., Greene, E. P., Liao, B., Shroff, S. & Thonhoff, J. R.
7/24/20 → 7/23/25
Project: Non Profit
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HEALEY ALS Platform Trial - Regimen-Specific Appendix C - For CNM-Au8
Appel, S. H., Greene, E. P., Liao, B., Shroff, S. & Thonhoff, J. R.
7/24/20 → 7/23/25
Project: Non Profit
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Dr. Appel_Biomarker Study_ALS and other Neurologic Diseases
Appel, S. H., Beers, D., Greene, E. P., Lai, E. C., Liao, B., Shroff, S., Thonhoff, J. R. & Zhao, W.
8/13/20 → …
Project: Clinical Trial
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Alexion ALXN1210-ALS-308 Appel
Appel, S. H., Greene, E. P., Shroff, S. & Thonhoff, J. R.
8/19/20 → …
Project: Clinical Trial
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HEALEY ALS Platform Trial - Regimen B Verdiperstat
Appel, S. H., Greene, E. P., Liao, B., Shroff, S. & Thonhoff, J. R.
8/19/20 → …
Project: Clinical Trial
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HEALEY ALS Platform Trial
Appel, S. H., Greene, E. P., Liao, B., Shroff, S. & Thonhoff, J. R.
8/19/20 → …
Project: Clinical Trial
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HEALEY ALS Platform Trial - Regimen C CNM-Au8
Appel, S. H., Greene, E. P., Liao, B., Shroff, S. & Thonhoff, J. R.
8/19/20 → …
Project: Clinical Trial
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HEALEY ALS Platform Trial - Regimen A Zilucoplan
Appel, S. H., Greene, E. P., Liao, B., Shroff, S. & Thonhoff, J. R.
8/20/20 → …
Project: Clinical Trial
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Radicava® (Edaravone) Findings in Biomarkers From ALS (REFINE-ALS)
Shroff, S., Appel, S. H., Greene, E. P. & Thonhoff, J. R.
10/20/20 → …
Project: Clinical Trial
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Phase 2a_AT-1501_ALS AT-1501-A201
Appel, S. H., Greene, E. P., Liao, B., Shroff, S. & Thonhoff, J. R.
10/30/20 → …
Project: Clinical Trial